Rocket Pharmaceuticals

Business Area(s): 


Description: 

Rocket's lentiviral-based programs aim to enable transduction of patients’ stem cells by means of 3rd-generation, self-inactivating lentiviral vectors to optimize the potential for gene-correction and stem cell engraftment such that the functional deficits of each disorder are corrected, with sufficient quantities of healthy protein manufactured by patients’ own hematopoietic cells. 

Location(s): 
New York NY
United States