Novartis
Small Molecules, Vaccines, Biologics, Novartis Gene Therapies develops and commercializes gene therapy products for neurological genetic diseases. One of Novartis' products is Zolgensma (AVXS-101), a gene therapy product for the treatment of spinal muscular atrophy. Novartis also makes Kymriah, an FDA-approved T cell based treatment for Lymphoblastic Leukemia and B-cell lymphoma.
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