Akcea is developing treatments for unaddressed or under-addressed serious and rare diseases with leading-edge, RNA-targeted medicines.
Arcturus Therapeutics Ltd. is a preclinical-stage biopharmaceutical company primarily focused on the discovery, development and commercialization of RNA medicines using proprietary lipid-mediated ...
Arrowhead Pharmaceuticals develops medicines that treat intractable diseases by silencing the genes that cause them. Using a broad portfolio of RNA chemistries and efficient modes of delivery, ...
Develops Enhanced CrossLinking and Immunoprecipitation (eCLIP), followed by high-throughput sequencing (eCLIP-seq), to identify RNA transcripts bound in vivo by a protein of interest.
mRNA based medicines for rare diseases
enGene Inc. has developed a highly flexible nucleotide (DNA and RNAi) delivery technology that targets mucosal tissues and can be used to treat numerous prevalent, chronic diseases via the ...
Ethris is paving a new path from genes to therapeutic proteins using our proprietary messenger RNA technologies. Their integrated platform enables the discovery, design and development of ...
Multivalent RNAi Platform, Delivery
Gene therapy requires delivery. Ligandal has developed a breakthrough nanotechnology for the precise and high-efficiency delivery of nucleic acids (CRISPR, TALEN, and RNA) to specific cells and ...
RNA Profiling and Services
A biopharmaceutical company developing a portfolio of mRNA products to correct inherited, life-threatening liver diseases in children.
PhaseRx is developing a portfolio of mRNA products to treat children with life-threatening inherited liver diseases.
Promosome was founded in 2003 to commercialize discoveries at The Scripps Research Institute by the late Nobel Laureate Dr. Gerald Edelman and his colleague Dr. Vincent Mauro, now Chief Scientific ...
Developing RNA-based therapeutics for rare diseases.
RAPiD GENOMICS offers customized, innovative genetic and genomic solutions for your unique applications.
Ribometrix is a platform therapeutics company discovering small molecule drugs that target functional 3D RNA structures to treat human diseases.
RTLGenomics is a full service sequencing company offering sequencing approaches including barcoding, metagenomics and transcriptomics. A sister lab, MicroGen, is a CAP accredited clinical ...
Seqll specializes in True Single Molecule Sequencing, DNA and RNA.
Designing of small molecules that target the RNA splicing process.