Genetic Disease Companies and Organizations

 

9 Organization(s)

American Gene Technologies

Business Area(s): 
Description: 

American Gene Technolgies is devleoping therapeutics based on lentiviral vectors to target HIV, PKU, Liver cancer, Parkinson's disease, and familial dysautonomia.

BioBlast Pharma

Business Area(s): 
Description: 

BioBlast Pharma manufactures Trehalose, a therapeutic to potentially treat a number of devastating PolyA/PolyQ diseases. Trehalose acts as a chemical chaperone to protects against pathological ...

Clementia Pharmaceuticals

Business Area(s): 
Description: 

Fibrodysplasia ossificans progressiva treatments

Confluence Pharmaceuticals

Business Area(s): 
Description: 

Autism and Fragile X Syndrome treatments

Exemplar Genetics

Business Area(s): 
Description: 

Exemplar Genetics develops specialized miniature swine models that are genetically engineered to exhibit a wide variety of human disease states, to provide a more accurate platform to test the ...

Genomics Medicine Ireland

Business Area(s): 
Description: 

Genomics Medicine Ireland is embarking on a multi-year, island-wide health discovery project which aims to build the largest, most comprehensive population-scale, disease-specific genomic study ...

KromaTiD

Business Area(s): 
Description: 

 

KromaTiD, Inc. provides products and services for mutation detection and disease diagnosis.  KromaTiD’s patented

...

Laurent Pharmaceuticals

Business Area(s): 
Description: 

Cystic Fibrosis treatment

SynapDx

Business Area(s): 
Description: 

Autism diagnosis

Don't see an employer? Please fill out the form