American Gene Technolgies is devleoping therapeutics based on lentiviral vectors to target HIV, PKU, Liver cancer, Parkinson's disease, and familial dysautonomia.
Viral Vector Therapeutics, Gene Therapy
Angionetics Inc., is a company focused on the late-stage clinical development and commercialization of Generx®, an angiogenic gene therapy product candidate designed for medical revascularization ...
Gene Therapy for Friedrich's ataxia
custom-made recombinant viral vectors
AAV Gene Therapy Treatments
Gene silencing technology
Adeno-Associated Virus Delivery, Gene Therapy
Gene therapies for rare and orphan neurological genetic diseases
Cellular & Gene Therapies
BEAT Biotherapeutics Corp. (BEATBio) is developing BB-R12, a novel gene therapy with the potential to revolutionize the treatment of heart failure.
Develops next-generation product candidates in some of the most important areas of cellular immunotherapy, including hematopoietic stem cell transplantation (HSCT), CAR T cell therapy, and TCR ...
A biopharmaceutical company. They discover, develop, and deliver medicines to treat serious disease.
Designing next generation immunotherapies based on gene-edited CAR T-cells
Genetically targeted medicine
Viral Vectors & Gene Therapy
Gene Therapy, Orphan Diseases
Gene Transfer Technology
Ophthalmic Gene Therapy
Gene Therapy platform technology
Gene Therapy for Cancer
Engineers B cells through gene therapy to produce proteins that combat disease.
Gene and Immunotherapies
AAV gene therapy technology
Gene Therapy or 'genomic medicine'
Gene therapy cancer treatment
Gene therapies for retinal dystrophies
Gene shuffling technology
Site-Specific Gene Modification System
Plasmid and Adenovirus Purification
Gene Therapy, Biologics
Sangamo was founded in 1995 as Sangamo BioSciences, Inc. in order to research new technologies for genome editing. Over two decades, Sangamo's scientists developed the most advanced, flexible and ...
We are Sarepta Therapeutics: a biopharmaceutical company focused on developing innovative RNA-targeted therapeutics. Our goal is to harness the power of cutting-edge technology
Spark Therapeutics makes Luxturna, a form of gene therapy that treats Leber congenital amaurosis—a rare, inherited form of childhood blindness.
Gene Therapy, Agribiotech, Biotech Lab Technology
Gene & Cell Therapy Services
Uses recombinant Adeno-associated virus to engineer and edit genomes and make universal donor cells.
Gene Delivery, Services