Gene Therapy Companies and Organizations

 

57 Organization(s)

4D Molecular Therapeutics

Business Area(s): 
Description: 

Gene Therapy

AGTC

Business Area(s): 
Description: 

Gene Therapy

American Gene Technologies

Business Area(s): 
Description: 

American Gene Technolgies is devleoping therapeutics based on lentiviral vectors to target HIV, PKU, Liver cancer, Parkinson's disease, and familial dysautonomia.

AmpliPhi Biosciences

Business Area(s): 
Description: 

Viral Vector Therapeutics, Gene Therapy

AnGes

Business Area(s): 
Description: 

Gene therapy

Angionetics

Business Area(s): 
Description: 

Angionetics Inc., is a company focused on the late-stage clinical development and commercialization of Generx®, an angiogenic gene therapy product candidate designed for medical revascularization ...

Annapurna

Business Area(s): 
Description: 

Gene Therapy for Friedrich's ataxia

Applied Viromics

Business Area(s): 
Description: 

custom-made recombinant viral vectors

Audentes Therapeutics

Business Area(s): 
Description: 

AAV Gene Therapy Treatments

Aum LifeTech

Business Area(s): 
Description: 

Gene silencing technology

Avalanche Biotechnologies

Business Area(s): 
Description: 

Adeno-Associated Virus Delivery, Gene Therapy

AveXis

Business Area(s): 
Description: 

Gene therapies for rare and orphan neurological genetic diseases

Avrobio

Business Area(s): 
Description: 

Cellular & Gene Therapies

BEAT BioTherapeutics

Business Area(s): 
Description: 

BEAT Biotherapeutics Corp. (BEATBio) is developing BB-R12, a novel gene therapy with the potential to revolutionize the treatment of heart failure.

Bellicum Pharmaceuticals

Business Area(s): 
Description: 

Develops next-generation product candidates in some of the most important areas of cellular immunotherapy, including hematopoietic stem cell transplantation (HSCT), CAR T cell therapy, and TCR ...

Bristol-Myers Squibb

Business Area(s): 
Description: 

A biopharmaceutical company.  They discover, develop, and deliver medicines to treat serious disease.

CALiMMUNE

Business Area(s): 
Description: 

Gene Therapy

Cellectis

Business Area(s): 
Description: 

Designing next generation immunotherapies based on gene-edited CAR T-cells

Cellomics

Business Area(s): 
Description: 

Lentiviral vectors

DalCor Pharmaceuticals

Business Area(s): 
Description: 

Genetically targeted medicine

Dimension Therapeutics

Business Area(s): 
Description: 

Gene Therapy

Discovery Genomics (Immusoft)

Business Area(s): 
Description: 

Gene Therapy

DNAVEC

Business Area(s): 
Description: 

Viral Vectors & Gene Therapy

Errant Gene Therapeutics

Business Area(s): 
Description: 

Gene Therapy, Orphan Diseases

FIT Biotech

Business Area(s): 
Description: 

Gene Therapy

GeneCure Biotechnologies

Business Area(s): 
Description: 

Gene Transfer Technology

Genethon

Business Area(s): 
Description: 

Gene Therapy

GenSight Biologics

Business Area(s): 
Description: 

Ophthalmic Gene Therapy

GenVec

Business Area(s): 
Description: 

Gene Therapy

Global BioTherapeutics

Business Area(s): 
Description: 

Gene Therapy platform technology

HORAMA

Business Area(s): 
Description: 
HORAMA is developing innovative gene therapy medicinal products in the field of rare ophthalmological diseases to preserve visual autonomy of the affected patients. 

iCell Gene Therapeutics

Business Area(s): 
Description: 

Gene Therapy for Cancer

Immusoft

Business Area(s): 
Description: 

Engineers B cells through gene therapy to produce proteins that combat disease.

InvivoGen Therapeutics

Business Area(s): 
Description: 

Gene and Immunotherapies

Lysogene

Business Area(s): 
Description: 

AAV gene therapy technology

Medgenics

Business Area(s): 
Description: 

Gene Therapy or 'genomic medicine'

Milo Biotechnology

Business Area(s): 
Description: 

Gene Therapy

MultiVir

Business Area(s): 
Description: 

Gene therapy cancer treatment

NightstaRx

Business Area(s): 
Description: 

Gene therapies for retinal dystrophies

Novahep

Business Area(s): 
Description: 

Gene Therapy

Novici Biotech

Business Area(s): 
Description: 

Gene shuffling technology

Nucelis

Business Area(s): 
Description: 

Site-Specific Gene Modification System

Oxford Biomedica

Business Area(s): 
Description: 

Gene-based Medicines

Puresyn

Business Area(s): 
Description: 

Plasmid and Adenovirus Purification

ReGenX Biosciences

Business Area(s): 
Description: 

Gene Therapy, Biologics

Renova Therapeutics

Business Area(s): 
Description: 

Gene Therapy

RetroSense Therapeutics

Business Area(s): 
Description: 

Gene Therapy

Sangamo Therapeutics

Business Area(s): 
Description: 

Sangamo was founded in 1995 as Sangamo BioSciences, Inc. in order to research new technologies for genome editing. Over two decades, Sangamo's scientists developed the most advanced, flexible and ...

Sarepta Therapeutics

Business Area(s): 
Description: 

We are Sarepta Therapeutics: a biopharmaceutical company focused on developing innovative RNA-targeted therapeutics.  Our goal is to harness the power of cutting-edge technology 
to ...

Spark Therapeutics

Business Area(s): 
Description: 

Spark Therapeutics makes Luxturna, a form of gene therapy that treats Leber congenital amaurosis—a rare, inherited form of childhood blindness.

Takara Bio

Business Area(s): 
Description: 

Gene Therapy, Agribiotech, Biotech Lab Technology

TrakCel

Business Area(s): 
Description: 

Gene & Cell Therapy Services

Transgene

Business Area(s): 
Description: 

Viral Vector Therapeutics, Gene Therapy

uniQure

Business Area(s): 
Description: 

Gene Therapy

Universal Cells

Business Area(s): 
Description: 

Uses recombinant Adeno-associated virus to engineer and edit genomes and make universal donor cells.

Vectalys

Business Area(s): 
Description: 

Gene Delivery, Services